好色先生

好色先生

Explore the latest content from across our publications

Log In

Forgot Password?
Create New Account

Loading... please wait

Abstract Details

Familial MuSK Myasthenia Gravis
Neuromuscular and Clinical Neurophysiology (EMG)
P3 - Poster Session 3 (12:00 PM-1:00 PM)
1-008
Describe two siblings with MUSK+ Myasthenia Gravis

There are several reports of ACHR + Familial Myasthenia Gravis (Honeybourne at al.1982; Chin et al.1985 and Evoli et al. 1995)  No MuSK+ cases have been reported.

CASE HISTORY 1:  a 34 year old right handed African American female developed intermittent horizontal diplopia followed by weekly recurrent gasping for air and choking while eating  Episodes resolved after 1-2 minutes. Initial diagnosis was asthma but inhaler gave no relief.  About 16 months later, ACHR antibody panel was negative. 
With continued episodes, MuSK antibody panel was positive at 1:2560.  Over 6 months, she further noted dysphagia, facial weakness, and persistent diplopia. Occasionally when drinking liquids, fluid came out her nose.  She developed neck and extremity weakness worse at end of day.  Trapezius 3 HZ repetitive nerve stimulation (RNS) demonstrated a 14% decrement. Chest CT was negative for thymoma but showed a small thyroid nodule.  She improved with initiation of prednisone 30 mg daily and Mestinon 60 mg daily. After several months  trapezius RNS demonstrated a 13.4% decrement and post activation exhaustion of 18.6%.  MMT was 26 and plasmapheresis produced resolution of symptoms at 1 month followup.   Cellcept 1000 mg BID was added and prednisone 60 daily continued with stable improvement.

CASE HISTORY 2:   A year prior to symptom onset of Case 1, her brother, a 31 year right handed male, developed similar episodic weakness including symptoms of fatigue late in the day. Workup yielded a negative ACHR antibody panel; however MuSK antibody panel was positive. His diagnosis and response to therapy led to the evaluation and treatment for his sister later that year.  He is stable by history and medical record review from another location.

NA
We describe the first report of familial MuSK+ (AChR-) myasthenia gravis in 2 siblings.
Authors/Disclosures
Janice M. Massey, MD, FAAN (Duke University Medical Center)
PRESENTER
Dr. Massey has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Argenix. Dr. Massey has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Revance Therapeutics. Dr. Massey has received personal compensation in the range of $500-$4,999 for serving on a Scientific Advisory or Data Safety Monitoring board for Momenta. The institution of Dr. Massey has received research support from Revance .
E. W. Massey, MD, FAAN (Duke university Medical Center) No disclosure on file