Abstract Details

Title Response to Enzyme Replacement Therapy in 18 Juvenile and Adult Patients with Severe Pompe Disease

Topic Muscle Disease/Neuromuscular Junction

Presentation(s) (-)

Poster/Presentation
Number 003

Objective

Background

Design/Methods

Results

Conclusions

Authors/Disclosures
Ans Van Der Ploeg (Metabolic Disease and Genetics, Erasmus Medic)	The institution of Ans Van Der Ploeg has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Sanofi Genzyme . The institution of Ans Van Der Ploeg has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Amicus. The institution of Ans Van Der Ploeg has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Spark Therapeutics . The institution of Ans Van Der Ploeg has received research support from Sanofi Genzyme.
Deborah Marsden (Genzyme)	No disclosure on file
	No disclosure on file
	No disclosure on file

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