2026 Annual Meeting | SP3 - Society Spotlight: American Society for Gene and Cell Therapy
| 03:30 PM - 03:50 PM CDT | Speaker |
Computational Modeling and Preclinical Evidence Supporting LTS-201, an MSH3-Lowering Therapy for Huntington’s Disease
Bryan Simpson, PhD |
| 03:50 PM - 04:10 PM CDT | Speaker |
Molecular and Behavioral Rescue Following Dual AAV Targeted CRISPR Epigenome Editing in CDKL5 Deficiency Disorder Patient-Derived Organoids and Transgenic Mice
Julian Halmai, PhD, MSc |
| 04:10 PM - 04:30 PM CDT | Speaker |
Investigator-initiated Development Paths for Oligonucleotide and Epigenetic Therapies in Prion Disease
Sonia M. Vallabh, PhD |
| 04:30 PM - 04:50 PM CDT | Speaker |
Enabling CNS Gene Therapies with AAV Capsid Engineering
Benjamin Deverman, PhD |
| 04:50 PM - 05:10 PM CDT | Speaker |
Four Year Follow-up of AAV-mediated Gene Replacement Therapy in a Large Animal Model of Krabbe Disease
Allison M. Bradbury, PhD |
| 05:10 PM - 05:30 PM CDT | Speaker |
Widespread CNS Delivery with Best-in-class Liver Detargeting Following Intravenous Injection of a Novel AAV
Mugdha Deshpande, PhD |
| Steven Gray, PhD | No disclosure on file |
| Sonia M. Vallabh, PhD | An immediate family member of Dr. Vallabh has received personal compensation in the range of $50,000-$99,999 for serving as a Consultant for Deerfield. Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Alnylam Pharmaceuticals. An immediate family member of Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving as a Consultant for Alnylam Pharmaceuticals. An immediate family member of Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Abbvie. An immediate family member of Dr. Vallabh has received personal compensation in the range of $10,000-$49,999 for serving on a Speakers Bureau for Eli Lilly & Co.. An immediate family member of Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Vertex. An immediate family member of Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Voyager Theapeutics. Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Abbvie. Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Eli Lilly & Co.. Dr. Vallabh has received personal compensation in the range of $500-$4,999 for serving on a Speakers Bureau for Voyager Therapeutics. The institution of Dr. Vallabh has received research support from Eli Lilly & Co.. The institution of Dr. Vallabh has received research support from Gate Bioscience. The institution of Dr. Vallabh has received research support from Ionis Pharmaceuticals. The institution of Dr. Vallabh has received research support from Sangamo. Dr. Vallabh has a non-compensated relationship as a President with Prion Alliance that is relevant to AAN interests or activities. |
| Bryan Simpson, PhD | Dr. Simpson has received personal compensation for serving as an employee of Latus Bio. Dr. Simpson has or had stock in Latus Bio. |
| Julian Halmai, PhD, MSc | Dr. Halmai has nothing to disclose. |
| Benjamin Deverman, PhD | No disclosure on file |
| Allison M. Bradbury, PhD | Dr. Bradbury has received intellectual property interests from a discovery or technology relating to health care. |
| Mugdha Deshpande, PhD | Dr. Deshpande has received personal compensation for serving as an employee of Dyno Therapeutics. |